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orphan drugs

Orphan Drugs as Strategic Assets: Lifecycle Patterns, Sales Resilience, and Market Impact

Orphan drugs Sales Resilience Lifecycle Patterns

This analysis refutes the misconception of orphan drugs as niche products. Using 2025 Q1 sales data and lifecycle patterns, it demonstrates their long-term revenue resilience and strategic portfolio value.

September 12, 2025 by N55.6761

Piramal Pharma Solutions to join hands with Epirium Bio to develop and manufacture orphan drugs

Piramal Pharma Solutions Epirium Bio orphan drugs

The integrated programme, involving three Piramal Pharma Solutions sites, encompasses formulation development, supply of APIs and intermediates, chemistry development and manufacturing, and solid oral dosage form drug product.

August 28, 2020 by expresspharma

Orphan drugs face uphill battle in 2020: GlobalData

ODD orphan drugs FDA EMA

ODDs have been a focus of interest from the pharma industry for many years, with many companies enticed by the benefits of the enhanced regulatory processes, tax benefits and extended market exclusivity.

March 3, 2020 by expresspharma

Biologics or small molecule drugs for rare disease treatment? It is a question

rare diseases orphan drugs biologics small molecule drugs

To both patients and pharmaceutical practitioners, it is a question as to whether to choose biologics or small molecule drugs for rare disease treatment, since the prices are sky-high.

July 31, 2019 by PharmaSources/Miling

Little Orphan Drugs Can Lead to Big Market Rare Disease Drugs in China

orphan drugs Rare Disease

In the Ice Bucket Challenge in 2014, the “amyotrophic lateral sclerosis” (ALS) patients attracted the world’s attention, and more people started to pay attention to the rare diseases.

January 22, 2018 by zhulikou431

Rare disease in EU

orphan drugs Rare Disease

According to some information released by the European Medicines Agency (EMA), there are about 30 million people in Europe suffering from rare diseases, the incidence of most diseases less than one hundred thousandth.

January 9, 2018 by Zhulikou431

Rare disease in America

orphan drugs Rare Disease

Rare disease is a general term for a group of diseases with a very low incidence, also known as orphan disease.

January 9, 2018 by Zhulikou431

Rhizen receives US FDA orphan drug designation

Rhizen orphan drugs

The US Food and Drug Administration (US FDA) has granted orphan drug designation for Tenalisib (RP6530) for the treatment of patients with peripheral T-cell lymphoma (PTCL), Alembic Pharmaceuticals said in a BSE filing.

December 27, 2017 by expressbpd

FDA grants orphan drug status to Shire’s UC treatment SHP647

FDA Shire orphan drugs

FDA has granted orphan drug designation to Shire’s investigational mucosal addressin cell adhesion molecule-1 antibody, SHP647, for the treatment of paediatric patients with moderately to severely active ulcerative colitis

December 4, 2017 by pharmaceutical-technology

GST makes ‘orphan drugs’ prices soar

orphan drugs GST

MUMBAI: Prices of exorbitantly-priced life-saving medicines, used to treat rare diseases have increased by 12%, with implementation of Goods and Services Tax, resulting in skyrocketing bills and leaving many patients in the lurch.

November 27, 2017 by indiatimes

GNH India clears audit to trade orphan drugs with UK

GNH India orphan drugs UK

Orphan drugs such as Ferripox, Raxone, Trientine and Mitocin will now available to the Indian population.

July 11, 2017 by expressbpd

Orphan drugs become the new favorite of pharmaceutical industry upon the huge market potential

orphan drugs Pharmaceutical industry

FDA approved the marketing application of Merck Serono’s Avelumab through accelerated approval on March 23, 2017, which can be said to ignite the medical circle and again draws the public interest in words like “orphan drug” and “rare disease”.

April 7, 2017 by en-cphi.cn